[HTML][HTML] Development of novel NEMO-binding domain mimetics for inhibiting IKK/NF-κB activation

J Zhao, L Zhang, X Mu, C Doebelin, W Nguyen… - PLoS …, 2018 - journals.plos.org
J Zhao, L Zhang, X Mu, C Doebelin, W Nguyen, C Wallace, DP Reay, SJ McGowan, L Corbo
PLoS biology, 2018journals.plos.org
Nuclear factor κB (NF-κB) is a transcription factor important for regulating innate and
adaptive immunity, cellular proliferation, apoptosis, and senescence. Dysregulation of NF-κB
and its upstream regulator IκB kinase (IKK) contributes to the pathogenesis of multiple
inflammatory and degenerative diseases as well as cancer. An 11–amino acid peptide
containing the NF-κB essential modulator (NEMO)-binding domain (NBD) derived from the C-
terminus of β subunit of IKK, functions as a highly selective inhibitor of the IKK complex by …
Nuclear factor κB (NF-κB) is a transcription factor important for regulating innate and adaptive immunity, cellular proliferation, apoptosis, and senescence. Dysregulation of NF-κB and its upstream regulator IκB kinase (IKK) contributes to the pathogenesis of multiple inflammatory and degenerative diseases as well as cancer. An 11–amino acid peptide containing the NF-κB essential modulator (NEMO)-binding domain (NBD) derived from the C-terminus of β subunit of IKK, functions as a highly selective inhibitor of the IKK complex by disrupting the association of IKKβ and the IKKγ subunit NEMO. A structure-based pharmacophore model was developed to identify NBD mimetics by in silico screening. Two optimized lead NBD mimetics, SR12343 and SR12460, inhibited tumor necrosis factor α (TNF-α)- and lipopolysaccharide (LPS)-induced NF-κB activation by blocking the interaction between IKKβ and NEMO and suppressed LPS-induced acute pulmonary inflammation in mice. Chronic treatment of a mouse model of Duchenne muscular dystrophy (DMD) with SR12343 and SR12460 attenuated inflammatory infiltration, necrosis and muscle degeneration, demonstrating that these small-molecule NBD mimetics are potential therapeutics for inflammatory and degenerative diseases.
PLOS